Review on Development of Orphan Drug for Rare Disease

  • Posted on: 1 August 2014
  • By: admin

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PharmaTutor (August- 2014)
ISSN: 2347 - 7881
(Volume 2, Issue 8)


Received On: 16/05/2014; Accepted On: 15/06/2014; Published On: 01/08/2014


AUTHORS: Kamshette Sharada*, Poul Bhagwat, Ghodke Amol
Department of Quality Assurance,
Maharashtra College of Pharmacy,
Nilanga, Maharashtra, India.


Simply receiving a diagnosis of a rare disease often becomes a frustrating quest, since many doctors may have never before heard of or seen the disease. This is, however, a time of great progress and hope. Biopharmaceutical research is entering an exciting new era with a growing understanding of the human genome. Scientific advances have given researchers new tools to explore rare diseases, which are often more complex than common diseases.
“Who else has this rare disease? How many of us are there? What can I expect now? What is known or not known about this disease?” These are among the questions that patients and family members ask as they become, out of necessity, advocates for themselves or others.


How to cite this article: S Kamshette, B Poul, A Ghodke; Review on Development of Orphan Drug for Rare Disease; PharmaTutor; 2014; 2(8); 66-72